Cell and Gene Therapy

Enabling the Future of Cell & Gene Therapies through Non Proprietary Patient-Owned Data Collection

March 16, 2021

herapies through Non Proprietary
Cell and gene therapies have emerged as a new treatment paradigm, and with them has come the potential
to alter the course of many rare diseases. In many cases, there is an opportunity to correct the underlying
dysfunction with a one-time administration of a therapy and provide either a functional cure or a substantial
improvement in health outcomes. In other cases, long term symptom relief will be the primary therapeutic
objective. Some of these indications may require more than one dose to achieve continued symptom relief
and scientists and companies are working on technologies that will enable the use of a repeat dose.

Spotlight

NG BIOTECH

NG Biotech is providing Real-Time Test Results and has developed whole blood rapid tests for optimization of patient screening and monitoring.

OTHER WHITEPAPERS
news image

Bold Goals for U.S. Biotechnology and Biomanufacturing

whitePaper | March 22, 2023

The world is on the cusp of an industrial revolution fueled by biotechnology and biomanufacturing. Emerging biological technologies are and will continue to transform the foundation of our physical world – everything from clothing, to plastics, to fuels, to concrete.

Read More
news image

Further Discussion on Plasmids to Establish Release Specifications Using a Risk-Based Approach to Manage Supply

whitePaper | December 6, 2022

BioPhorum’s mission is to create environments where the global biopharmaceutical industry can collaborate and accelerate its rate of progress, for the benefit of all.

Read More
news image

New Diagnostic Approaches for Undiagnosed Rare Genetic Diseases

whitePaper | April 16, 2020

Accurate diagnosis is the cornerstone of medicine; it is essential for informed care and promoting patient and family well-being. However, families with a rare genetic disease (RGD) often spend more than five years on a diagnostic odyssey of specialist visits and invasive testing that is lengthy, costly, and often futile, as 50% of patients do not receive a molecular diagnosis.

Read More
news image

The EU Clinical Trials Regulation − What You Need to Know

whitePaper | March 22, 2022

The Clinical Trials Regulation has retained some definitions and refined others. For example the definition of “clinical study”: “Any investigation in relation to humans intended: (a) to discover or verify the clinical, pharmacological or other pharmacodynamic.

Read More
news image

Validation of ICON™ Automated Cell Counting and Viability Assay

whitePaper | August 10, 2022

Determination of cell viability and concentration using trypan blue exclusion is essential for biotherapeutic workflows, enabling optimisation of protocols, monitoring of changes to the culture environment, and selection of the best clones for culture progression.

Read More
news image

Biopharmaceutical Sector

whitePaper | May 29, 2023

tronger than expected US inflation and a bump in consumer spending have fuelled worldwide expectations that interest rates will go higher, as predictions about future monetary policy rapidly shift.

Read More

Spotlight

NG BIOTECH

NG Biotech is providing Real-Time Test Results and has developed whole blood rapid tests for optimization of patient screening and monitoring.

Events