What is Gene Therapy?

December 19, 2017

Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery. Researchers are testing several approaches to gene therapy, including: Replacing a mutated gene that causes disease with a healthy copy of the gene.

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Xell AG

Xell is an experienced partner for companies in the biotech and pharmaceutical industry providing them with highly-efficient solutions in cell culture technology. Meeting our customers’ specific needs is the objective of our dedicated team – our personal approach to challenging tasks is key to Xell’s success. With years of industry experience, we bring our extensive expertise in ultra-high performance media and feed development, and apply our powerful analytical tools for in-depth characterization of biological systems and pharmaceutical proteins, guaranteeing optimal solutions for our customers’ bioprocesses.

OTHER VIDEOS

What is Genomic Medicine?

video | June 16, 2022

Our DNA contains 3 billion letters of code: our genome. Almost 99.8% is the same for everyone, but in the remaining 0.2% there are differences that can sometimes be harmful. With genomic medicine we can have our DNA analysed to look for these differences to inform and personalise our healthcare. Genomics England’s vision is to support the NHS to make genomic medicine available to every patient, whilst enabling researchers to improve our understanding of diseases....

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Peptides From Phage Display Library Modulate Gene Expression In Mesenchymal Cells

video | June 8, 2022

Peptides from Phage Display Library Modulate Gene Expression in Mesenchymal Cells and Potentiate Osteogenesis in Unicortical Bone Defects - a 2 minute Preview of the Experimental Protocol Gary Balian, Gina Beck, Vedavathi Madhu, Robert Sikes, Quanjun Cui, Haixiang Liang, Joshua Bush University of Virginia, Orthopaedics Research; University of Delaware, Biological Sciences; University of Virginia, Orthopaedic Surgery; A phage display library was used to identify peptide sequences that target bone. The objective was to investigate the effect of these peptides on mesenchymal cell differentiation and to determine their effect on bone regeneration....

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Would a society based on genetics be… good?

video | June 15, 2022

Eugenics is the practice of using "planned breeding" for "racial improvement." Because this idea is repulsive, the predominant response has been "genome blindness” — that is, avoiding any study or discussion of genetic differences between people. But according to geneticist Paige Harden, this is the wrong solution. Instead, we should identify genetic differences between people — including those that might affect social outcomes — so that we can help provide people with the resources they need to be successful....

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mRNA Therapy for Fragile X Syndrome

video | June 2, 2022

Dr. Kathryn Whitehead, Associate Professor at Carnegie Mellon University, helped develop the revolutionary science behind the COVID-19 vaccines. With a 2 year $100,000 grant from FRAXA, her team will now adapt mRNA technology to deliver the missing Fragile X protein, to treat people who have Fragile X syndrome....

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Spotlight

Xell AG

Xell is an experienced partner for companies in the biotech and pharmaceutical industry providing them with highly-efficient solutions in cell culture technology. Meeting our customers’ specific needs is the objective of our dedicated team – our personal approach to challenging tasks is key to Xell’s success. With years of industry experience, we bring our extensive expertise in ultra-high performance media and feed development, and apply our powerful analytical tools for in-depth characterization of biological systems and pharmaceutical proteins, guaranteeing optimal solutions for our customers’ bioprocesses.

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