Takeda Inks Licensing Option Agreement with Gene Editing Platform Developer Emendo

genengnews | April 24, 2019

Takeda Pharmaceutical has advanced further into gene editing, inking a licensing option agreement with and, through its venture capital arm, investing in Emendo Biotherapeutics, the gene editing discovery platform developer said today. The value of the agreement and the investment were not disclosed. Through the licensing option agreement, Emendo has granted Takeda the option to use its proprietary nuclease program OMNI to edit two genes as part of the pharma’s R&D efforts to treat unspecified genetic disorders. Headquartered in New York City, with an R&D center in Ness-Ziona, Israel, Emendo focuses on engineering site-specific nucleases for an accurate, sequence-specific and efficient correction mechanism that is homology-directed repair (HDR) mediated, and effective in post-mitotic cells. Emendo uses proprietary protein engineering and selection platforms that are designed to generate ultra-specific and highly active CRISPR OMNI nucleases.

Spotlight

For laboratories that must comply with Good Laboratory Practices (GLP), Good Manufacturing Practices (GMP), and Good Automated Manufacturing Practices (GAMP) regulations, it is important to have records or documented evidence of all relevant analyses reviewed by a second person and readily available for audits. Storing the result is not enough - each result set has to be complete and contain all relevant metadata.

Spotlight

For laboratories that must comply with Good Laboratory Practices (GLP), Good Manufacturing Practices (GMP), and Good Automated Manufacturing Practices (GAMP) regulations, it is important to have records or documented evidence of all relevant analyses reviewed by a second person and readily available for audits. Storing the result is not enough - each result set has to be complete and contain all relevant metadata.

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