Sangamo Therapeutics Announces Presentations At 2019 Annual Meeting Of The American Society Of Gene & Cell Therapy

Prnewswire | April 15, 2019

A  genomic medicine company, today announced that Sangamo scientists and collaborators will present data from the Company's clinical and preclinical pipeline at the 22nd Annual Meeting of the American Society of Gene & Cell Therapy (ASGCT) being held April 29th to May 2nd, 2019 in Washington, D.C. Abstracts accepted for presentation highlight data from the Company's gene therapy program in Fabry disease; ex vivogene-edited cell therapy programs in hemoglobinopathies being developed in partnership with Sanofi; and preclinical programs for CNS diseases using Sangamo's gene regulation approach, which include tauopathies, C9ORF72-linked ALS in collaboration with Pfizer, and Huntington's disease in collaboration with Takeda. "Sangamo's strong scientific presence at ASGCT demonstrates the breadth of our therapeutic pipeline and our expertise in innovative genomic medicines research and development," said Adrian Woolfson, M.D., Ph.D., Sangamo's Executive Vice President of Research and Development. "Through our pioneering work in developing zinc fingers for ex vivo and in vivo genome editing, we've gained invaluable insights into AAV manufacturing and delivery, as well as gene editing precision, efficiency, and specificity. We're now applying these insights to our integrated portfolio of programs in both gene therapy and ex vivo cell therapy as well as to our new zinc finger protein transcription factor gene regulation platform, which will be showcased at this year's meeting."

Spotlight

As the European population rapidly ages, the growing number of seniors with age-related chronic diseases presents a challenge to European societies and health care systems. DO-HEALTH is Europe's largest clinical trial in support of health at an older age and is a large, three-year multi-centre clinical trial that will generate needed efficacy and safety data for three interventions in the prevention of age-related diseases in seniors.

Spotlight

As the European population rapidly ages, the growing number of seniors with age-related chronic diseases presents a challenge to European societies and health care systems. DO-HEALTH is Europe's largest clinical trial in support of health at an older age and is a large, three-year multi-centre clinical trial that will generate needed efficacy and safety data for three interventions in the prevention of age-related diseases in seniors.

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